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Tell Us About LogicBio

Tell us about LogicBio Fred Chereau is the president and CEO of LogicBio Therapeutics, a biotechnology company in Cambridge, Mass., that is advancing an investigational therapy for methylmalonic acidemia(MMA). We sat down with him to talk about his work. Tell

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Help us teach physicians about organic acidemias

Help us teach physicians about organic acidemias FACT!  Teaching about metabolic diseases in medical school and residency programs is poor.FACT!  Most patients live and die without a diagnosis being made, especially when the disease presents in adulthood.FACT!  Patients cannot access effective therapies unless

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Hemoshear Insight Study

MMA & PA Insight Study HemoShear Therapeutics HemoShear Therapeutics Receives FDA Fast Track and Rare Pediatric Disease Designations for HST5040 to Treat Methylmalonic Acidemia and Propionic Acidemia ​​HemoShear Therapeutics Receives FDA Clearance of IND for Phase 2 Study of its

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PA Consensus Conference Articles

PA Consensus Conference Articles Reprinted from MOLECULAR GENETICS AND METABOLISM, Vol 105, No 1, 2012 with permission from Elsevier Reprinted from MOLECULAR GENETICS AND METABOLISM, Vol 105, No 1, 2012, pp 3-4, Kimberly A. Chapman, Marshall L. Summar, “Propionic Acidemia Consensus

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