Glutaric Aciduria Type 1 Natural History Study

 

Dr. Curtis Coughlin is partnering with a pharmaceutical company to conduct a natural history study of glutaric aciduria type 1 (GA-1). The goal of this study is to better understand this disorder and generate clinical data that can support the development of new therapies.

 

Progress in treatment development has been limited by the lack of comprehensive clinical data on GA-1. This study aims to address that gap by collecting patient health information that can guide future therapeutic research.

Watch Dr. Coughlin’s webinar to learn more about the study:
https://www.youtube.com/watch?v=_jyGNDjKpBA

 

For additional information about the GA-1 Natural History Study, visit:
https://ga1study.org/.

 

Select the “Express Interest” button on the website if you would like a member of the research team to contact you.